Variable | Adult cohort n = 106 | Pediatric cohort n = 19 | |
Valid results | 104 (98%) | 17 (90%) | |
Adult cohort n = 104 | Pediatric cohort n = 17 | ||
On-label options only | 3 (3%) | 0 | |
Off-label options only | 55 (53%) | 11 (65%) | |
Both on- and off- label options | 22 (21%) | 0 | |
Clinical Trial options | Phase I | 96 (92%) | 14 (82%) |
Phase II | 76 (73%) | 11 (65%) | |
Phase III | 11 (11%) | 0 |